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Type
Journal Article
Title

Are we prepared to deliver gene-targeted therapies for rare diseases?

Authors:

Author Name(s)
Timothy W. Yu
Stephen F. Kingsmore
Robert C. Green
Tippi MacKenzie
Melissa Wasserstein
Michele Caggana
Nina B. Gold
Annie Kennedy
Priya S. Kishnani
Matthew Might
Phillip J. Brooks
Jill A. Morris
Melissa A. Parisi
Tiina K. Urv

Year:

Date
2023
Journal Book Publisher Name
American Journal of Medical Genetics Part C: Seminars in Medical Genetics

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