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Publication
The cost of biotech innovation: Exploring research and development costs of cell and gene therapies
Molecular Therapy - Methods & Clinical Development -
Publication
The Landscape of Cellular and Gene Therapy Products: Authorization, Discontinuations, and Cost
Human Gene Therapy Clinical Development -
Publication
Medicaid coverage practices for approved gene and cell therapies: Existing barriers and proposed policy solutions
Molecular Therapy - Methods & Clinical DevelopmentAllen and colleagues describe how discrepancies between the legal requirement to cover all FDA-approved drugs according to their medically accepted indications and the coverage policies of 16… -
Collection
Paying for Cures: The Ethics and Economics of Gene Therapies for Rare Diseases
Rare diseases, most of which have a genetic basis, collectively affect an estimated 300 million individuals worldwide and are associated with significant morbidity and mortality. Although less than…- gene therapy
- sickle cell disease
- health economics
- nusinersen
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Video
Value and Values in Payment for Gene Therapies
The ELSI Friday Forum was held on May 12, 2023. Advances in gene therapies for monogenic disorders have brought hope of curative treatment. Since the Food and Drug Administration first approved a…- gene therapies
- cost of gene therapies
- payment
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Publication
Gene therapies: The challenge of super-high-cost treatments and how to pay for them
Regenerative Medicine -
Publication
Value-based pricing for emerging gene therapies: The economic case for a higher cost-effectiveness threshold
Journal of Managed Care & Specialty Pharmacy -
News
Value Ethics: Mapping Strategies for Value Assessment and Reimbursement of Targeted Genomic Therapies for Rare Diseases – A New CERA Working Group
CERA Working Groups are interdisciplinary teams that aim to deepen our understanding of emerging, high priority, or understudied ELSI issues using innovative approaches. CERA selects one or two…- genetic therapy
- cost of gene therapies
- working group
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Publication
Equitable access to gene therapy: A call to action for the American Society of Gene and Cell Therapy
Molecular Therapy -
Grant Abstract
Research, Treatment and Informed Consent in Gene Therapy
This project is designed to analyze the adequacy of the Belmont Report's distinction between research and treatment as a basis for informed consent policy especially as it pertains to gene…- behavioral /social science research tag
- Clinical Research
- Decision Making
- gene therapy
- health care policy